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Derniers dépôts
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Treatment
OPMD
Clinical trials
Alternative splicing
Myotonic dystrophy type 1
Male
Regeneration
Heart
Duchenne muscular dystrophy
Genotype phenotype correlation
Trinucleotide repeat expansion
CRISPRi
Cancer
Neuromuscular diseases
Dermatomyositis
Astrocyte
Myotonic Dystrophy type 1
Lamin A/C LMNA gene
Biomarker
Myoblasts
Errance diagnostique
Therapy
Humans
FSHD
Muscular dystrophy
Animals
Glutamate
Autoantibodies
Myopathy
CTG repeat contractions
PABPN1
COVID-19
Congenital myopathy
Heart failure
Aged
Motoneuron
Fabry disease
LMNA
Satellite cells
RNA interference
Transgenic mouse model
Inflammation
Neuromuscular disease
ALS
Myositis
Thérapie génique
Dilated cardiomyopathy
Neuromuscular junction
Fibrosis
Thymus
Diagnosis
Centronuclear myopathy
Mouse model
Laminopathie
AAV
Cell therapy
Myasthenia gravis
Antisense oligonucleotides
Mechanotransduction
Nuclear envelope
Aging
Cardiomyopathy
Becker muscular dystrophy
DMD
Myogenesis
Calcium
Rare diseases
Satellite cell
Transcriptomics
LMNA gene
RNA biology
Lamin A/C
Myotonic Dystrophy
Brain
Gene therapy
Laminopathy
Laminopathies
Myopathies
Outcome measures
Autoimmunity
Myotonic dystrophy
Biomarkers
Rare neuromuscular diseases
Myasthenia Gravis MG
Dynamin 2
Dystrophin
Muscle regeneration
Congenital muscular dystrophy
Long read sequencing
Muscle
Skeletal muscle
Exercise
Actin
MBNL
Amyotrophic lateral sclerosis
Cytokines
Cytoskeleton
Autoimmune diseases
Autophagy
CMS